ScienceMan with rare motor neuron disease reportedly improves after RNA therapy
Nature reports that the man was the first person to receive a drug designed to target the genetic mutation causing his disease.
TLDR
A man with an uncommon form of motor neuron disease experienced improved symptoms after receiving a drug designed to target the mutation causing his condition, Nature reports. He was the first person to receive the drug. Nature says gene-targeting treatments could also be used to treat other people with rare forms of amyotrophic lateral sclerosis (ALS).
Man with rare motor neuron disease reportedly improves after RNA therapy
Nature reports that the man was the first person to receive a drug designed to target the genetic mutation causing his disease.
TLDR
A man with an uncommon form of motor neuron disease experienced improved symptoms after receiving a drug designed to target the mutation causing his condition, Nature reports. He was the first person to receive the drug. Nature says gene-targeting treatments could also be used to treat other people with rare forms of amyotrophic lateral sclerosis (ALS).